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ADAR

ADAR ,全稱為腺苷脫氨酶作用于RNA 1,是RNA編輯的關(guān)鍵酶,能夠?qū)NA分子中的腺苷(A)轉(zhuǎn)化為肌苷(I),從而影響RNA的功能和編碼的蛋白質(zhì)。ADAR 蛋白在多種生物學(xué)過程中發(fā)揮重要作用,包括免疫反應(yīng)、神經(jīng)功能和疾病的發(fā)生發(fā)展。ADAR 蛋白相關(guān)疾病包括Aicardi-Goutières綜合征(AGS)和遺傳性對稱性色素異常癥(DSH),這些疾病都與RNA編輯異常有關(guān)。目前,針對ADAR蛋白的藥物研發(fā)主要集中在RNA編輯療法,旨在通過精確修飾RNA序列來治療遺傳疾病和復(fù)雜疾病。例如,斯坦福大學(xué)生物學(xué)家李進聯(lián)合創(chuàng)辦的RNA編輯療法公司AIRNA,正在開發(fā)針對Alpha-1抗胰蛋白酶缺乏癥(AATD)的RNA編輯療法,計劃于2025年進行I期臨床試驗。此外,其他公司如Wave Life Sciences和Korro Bio也在積極開發(fā)基于RNA編輯技術(shù)的藥物,為治療AATD等疾病帶來新的希望。

熱銷產(chǎn)品

Recombinant Human Double-stranded RNA-specific adenosine deaminase (ADAR), partial (CSB-EP001324HU)

驗證數(shù)據(jù)

CSB-EP001324HU

(Tris-Glycine gel) Discontinuous SDS-PAGE (reduced) with 5% enrichment gel and 15% separation gel.

ADAR Recombinant Monoclonal Antibody (CSB-RA906343A0HU)

驗證數(shù)據(jù)

CSB-RA906343A0HU

IHC image of CSB-RA906343A0HU diluted at 1:100 and staining in paraffin-embedded human brain tissue performed on a Leica BondTM system. After dewaxing and hydration, antigen retrieval was mediated by high pressure in a citrate buffer (pH 6.0). Section was blocked with 10% normal goat serum 30min at RT. Then primary antibody (1% BSA) was incubated at 4℃ overnight. The primary is detected by a Goat anti-rabbit IgG polymer labeled by HRP and visualized using 0.05% DAB.

ADAR Antibodies

ADAR for Homo sapiens (Human)